Research Partnerships
Entrepreneurship, innovation and engagement are an embedded part of our research culture. We focus on global and local economic and societal impact.
Developing new treatments for rare diseases
Developing treatments for rare diseases can be slow and expensive, leaving many conditions with limited treatment options.
Working with DEBRA, Queen Mary researchers have developed a new approach to rare-disease drug development that combines academic expertise, charity funding and patient-centred priorities.
The partnership has now reported its first research results, helping accelerate the search for treatments for people living with epidermolysis bullosa (EB), a rare life-limiting condition that causes extremely fragile skin to blister and tear at the slightest touch.
New approach to rare disease drug development